Sickle cell and beta thalassemia: what are the treatment options and challenges?
Sickle cell disorder and beta thalassemia are inherited blood conditions that can cause severe pain and organ damage. How are these conditions treated, and what challenges do patients face? What role could new personalised medicines like gene-editing therapies play, and what are the barriers to their adoption?
No abstract for this publication.
Publication type:
policy brief
Publication language:
English
Publication date:
2025-11
Publication URL:
https://doi.org/10.58248/PN754
Institute:
Parliamentary Office of Science and Technology of the UK Parliament (POST)
Country:
United Kingdom of Great Britain & Northern Ireland

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